1. Crispr editing machinery is packaged in ‘nanoparticles’ and injected into the patient
2. The nanoparticles are designed to find their way to the liver where the excess proteins are produced
Nanoparticles
2
3
Liver
1
3. They then locate the gene responsible for the overproduction within individual cells
4. At a cellular level the Crispr editing machinery locates the precise gene sequence responsible and disables it
Disables gene
4
1. Crispr editing machinery is packaged in ‘nanoparticles’ and injected into the patient
2. The nanoparticles are designed to find their way to the liver where the excess proteins are produced
3. They then locate the gene responsible for the overproduction within individual cells
4. At a cellular level the Crispr editing machinery locates the precise gene sequence responsible and disables it
Disables gene
Nanoparticles
4
2
3
1
Liver